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Eteplirsen Duchenne

Needless Delay for a Medicine That Could Save Kids' Lives

Tracy Seckler | Posted 05.05.2014 | Healthy Living
Tracy Seckler

My advisors tell me to keep working the system, to keep the door cracked open by giving FDA officials opportunities to "save face" and encourage a new drug application for eteplirsen. But I cannot allow any more time to go by.

Two Brothers Have Same Debilitating Condition, But Only One Approved For Experimental Drug

Posted 08.20.2012 | Healthy Living

Two Vermont brothers have the same debilitating condition -- Duchenne muscular dystrophy. Max Leclaire, 10, is on an experimental drug called eteplirs...