My advisors tell me to keep working the system, to keep the door cracked open by giving FDA officials opportunities to "save face" and encourage a new drug application for eteplirsen. But I cannot allow any more time to go by.
Read Whole Story
Two Vermont brothers have the same debilitating condition -- Duchenne muscular dystrophy. Max Leclaire, 10, is on an experimental drug called eteplirs...
Get top stories and blog posts emailed to me each day. Newsletters may offer personalized content or advertisements. Learn more.